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No Longer Night-Blind, Natalia Isn’t Afraid of the Dark

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After being treated with a breakthrough gene therapy at Children’s Hospital Los Angeles for a genetic eye disorder, 5-year-old Natalia can now see clearly for the first time in her life.

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‘I Can See! I Can See!’

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Trainee Spotlight: Leila Bahmani, PhD

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Since high school, Leila has been fascinated by how DNA molecules define our fundamental characteristics.

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What Is Gene Therapy?

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How next-generation gene therapies target the underlying causes of genetic diseases.

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As FDA Expands Approval of a New Gene Therapy to Treat Duchenne Muscular Dystrophy, a CHLA Expert Weighs in

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The new approval opens the gene therapy to a wider range of children with Duchenne muscular dystrophy, a rare genetic disorder that worsens over time.

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A Closer Look: Why Is Research Essential at a Children’s Hospital?

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The ambitions of pediatric researchers are global in scale: Beyond patients at their own hospital, they look to shape national and international standards for pediatric care.

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Research Staff Spotlight: Kayla Stepanian

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Originally training in ballet, Kayla Stepanian took on a role at CHLA and is now a Research Specialist working on research into inherited retinal diseases.

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Children’s Hospital Los Angeles and USC Announce the Creation of a $40 Million Collaboration for Pediatric Biomedical Research and Innovation

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The Initiative Will Benefit Innovative Studies and Projects Focused on Improving Children’s Health

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How Children’s Hospital Los Angeles Is Keeping Families Safe During COVID-19

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When Jenn and Mike Dupke had to take their 4-year-old son, Rhett, to Children’s Hospital Los Angeles for a week this spring—in the midst of the COVID-19 pandemic—they were nervous. Rhett has been

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