After receiving Hemgenix gene therapy at Children's Hospital Los Angeles, the 24-year-old is managing hemophilia B with no more infusions—and a newfound freedom.
At 4 years old, Eliot was the first patient at CHLA to receive Elevidys, a groundbreaking new gene therapy for Duchenne muscular dystrophy. The treatment has been a game changer for his health.
Born with grave cardiac defects, Aaliyah was dying. A CHLA heart surgeon devised a way to keep her alive for close to 500 days until a donor heart was found.
At age 9, Wallie and Noah were facing osteosarcoma—and a surgery that would change their lives forever. There was only one way to get through it: together.