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Research and Breakthroughs

What Is Gene Therapy?

August 26, 2024

How next-generation gene therapies target the underlying causes of genetic diseases.

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Research and Breakthroughs

New cGMP Facility Aims to Accelerate Cell Therapy for Pediatric Cancer

May 12, 2023

Four investigators share their research—and how the USC/CHLA facility will help bring novel cell therapies to clinical trials faster.

Press Release

Children’s Hospital Los Angeles and USC Announce the Creation of a $40 Million Collaboration for Pediatric Biomedical Research and Innovation

April 4, 2023

The Initiative Will Benefit Innovative Studies and Projects Focused on Improving Children’s Health

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Research and Breakthroughs

Study Targets Cisplatin Resistance in Pediatric Germ Cell Tumors

August 13, 2024

A CHLA oncologist is leading new research to improve outcomes for children, adolescents and young adults with relapsed or treatment-resistant germ cell tumors.

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Research and Breakthroughs

Can a Novel Approach Lead to Less-Toxic Treatments for Leukemia?

October 27, 2023

A new study finds that blocking Artemis significantly reduces the proliferation of leukemia cells, without affecting normal cells.

Press Release

Children’s Hospital Los Angeles Names James F. Amatruda, MD, PhD, as Director of the Cancer and Blood Disease Institute

August 13, 2024

LOS ANGELES (August 13, 2024) – Children’s Hospital Los Angeles has named James F. Amatruda, MD, PhD, a highly respected medical leader, clinician, and researcher with global recognitions, as Director

Laura Perin and Stefano Da Sacco with members of the GOFARR lab

Research and Breakthroughs

A Closer Look: Why Is Research Essential at a Children’s Hospital?

July 20, 2023

The ambitions of pediatric researchers are global in scale: Beyond patients at their own hospital, they look to shape national and international standards for pediatric care.

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Hospital News

100 Vision-Saving Procedures and Counting: Q&A With Retinal Gene Therapy Expert Dr. Aaron Nagiel 

November 27, 2024

A national leader in pediatric gene therapy, CHLA has treated more patients with the sight-saving Luxturna than any other center in the country.

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Our Patients

Can a New Way to Treat a Tumor Help Kai Beat Brain Cancer?

May 12, 2023

After her son was diagnosed with a rare tumor, Melissa searched for help. She found it at CHLA in the office of Dr. Ashley Margol, one of the few experts in an innovative therapy called MEMMAT.

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