What Is Gene Therapy?
August 26, 2024
How next-generation gene therapies target the underlying causes of genetic diseases.
Content related to Improving Access to Cell and Gene Therapy in Pediatrics
New cGMP Facility Aims to Accelerate Cell Therapy for Pediatric Cancer
May 12, 2023
Four investigators share their research—and how the USC/CHLA facility will help bring novel cell therapies to clinical trials faster.
Children’s Hospital Los Angeles and USC Announce the Creation of a $40 Million Collaboration for Pediatric Biomedical Research and Innovation
April 4, 2023
The Initiative Will Benefit Innovative Studies and Projects Focused on Improving Children’s Health
Children’s Hospital Los Angeles Names James F. Amatruda, MD, PhD, as Director of the Cancer and Blood Disease Institute
August 13, 2024
LOS ANGELES (August 13, 2024) – Children’s Hospital Los Angeles has named James F. Amatruda, MD, PhD, a highly respected medical leader, clinician, and researcher with global recognitions, as Director
Study Targets Cisplatin Resistance in Pediatric Germ Cell Tumors
August 13, 2024
A CHLA oncologist is leading new research to improve outcomes for children, adolescents and young adults with relapsed or treatment-resistant germ cell tumors.
Can a Novel Approach Lead to Less-Toxic Treatments for Leukemia?
October 27, 2023
A new study finds that blocking Artemis significantly reduces the proliferation of leukemia cells, without affecting normal cells.
Can a New Way to Treat a Tumor Help Kai Beat Brain Cancer?
May 12, 2023
After her son was diagnosed with a rare tumor, Melissa searched for help. She found it at CHLA in the office of Dr. Ashley Margol, one of the few experts in an innovative therapy called MEMMAT.
Gene Therapy Saves Greigh From a Paralyzing Muscle Disease
September 22, 2023
Newborn screening found that Greigh had spinal muscular atrophy. He was sent to Children’s Hospital Los Angeles, where gene therapy saved him from paralysis.
Will N-Acetylcysteine Be the Next Therapy to Prevent Cisplatin-Induced Hearing Loss?
July 24, 2023
A CHLA clinical trial finds that N-acetylcysteine may be a promising next-generation therapy to reduce the risk of cisplatin-induced hearing loss.