Our Patients Life With Hemophilia, Reimagined: Ryan's Gene Therapy Journey March 7, 2025 After receiving Hemgenix gene therapy at Children's Hospital Los Angeles, the 24-year-old is managing hemophilia B with no more infusions—and a newfound freedom. Read more
Research and Breakthroughs Elevidys Gene Therapy: A Neurologist’s Perspective November 7, 2024 A CHLA expert shares her experience of administering this gene therapy for Duchenne—and why comprehensive care is critical for patients. Read more
Leaning on her Love of Dance, Ella Faces a Challenging Cancer Treatment September 10, 2024 Performing TikTok routines with members of her care team has helped a teenage girl battle a rare kidney tumor. Read more