A CHLA expert shares her experience of administering this gene therapy for Duchenne—and why comprehensive care is critical for patients.

Performing TikTok routines with members of her care team has helped a teenage girl battle a rare kidney tumor.

It was an innocent question, one for which Meredith had the good fortune of not knowing the answer—otherwise she wouldn't have asked it: "What are labs?" After a week of fever for her 4-year-old